Clinical trial
A Phase 2, Open-Label Trial to Evaluate the Safety, Pharmacokinetics, Pharmacodynamics and Exploratory Clinical Activity of ALN-TTRSC in Patients With Transthyretin (TTR) Cardiac Amyloidosis
NCT01981837 is registered in ClinicalTrials.gov with Alnylam Pharmaceuticals as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 2, Open-Label Trial to Evaluate the Safety, Pharmacokinetics, Pharmacodynamics and Exploratory Clinical Activity of ALN-TTRSC in Patients With Transthyretin (TTR) Cardiac Amyloidosis
- Lead sponsor
- Alnylam Pharmaceuticals
- Phase
- Phase 2
- Overall status
- Completed
- Start date
- December 31, 2013
- Completion date
- January 31, 2015
- Enrollment
- 26 (actual)
- Sites
- 4
Conditions
As the registry lists them; a condition with its own page is linked.
ttr-mediated amyloidosis