Clinical trial
SIngle-Stage, Open-Label, Safety and Efficacy Study of Adeno-Associated Virus Encoding Human Aromatic L-Amino Acid Decarboxylase by Magnetic Resonance MR-guided Infusion Into Midbrain in Pediatric Patients With AADC Deficiency
NCT02852213 is registered in ClinicalTrials.gov with Krzysztof Bankiewicz as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- SIngle-Stage, Open-Label, Safety and Efficacy Study of Adeno-Associated Virus Encoding Human Aromatic L-Amino Acid Decarboxylase by Magnetic Resonance MR-guided Infusion Into Midbrain in Pediatric Patients With AADC Deficiency
- Lead sponsor
- Krzysztof Bankiewicz
- Phase
- Phase 1
- Overall status
- Recruiting
- Start date
- July 1, 2016
- Completion date
- August 31, 2037
- Enrollment
- 42 (estimated)
- Sites
- 3
Conditions
As the registry lists them; a condition with its own page is linked.
aadc deficiency