Clinical trial
An Open-Label Study Evaluating the Safety and Pharmacokinetics of Ataluren in Children From ≥6 Months to <2 Years of Age With Nonsense Mutation Duchenne Muscular Dystrophy
NCT04336826 is registered in ClinicalTrials.gov with PTC Therapeutics as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- An Open-Label Study Evaluating the Safety and Pharmacokinetics of Ataluren in Children From ≥6 Months to <2 Years of Age With Nonsense Mutation Duchenne Muscular Dystrophy
- Lead sponsor
- PTC Therapeutics
- Phase
- Phase 2
- Overall status
- Completed
- Start date
- December 29, 2021
- Completion date
- August 7, 2023
- Enrollment
- 6 (actual)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
nonsene mutation duchenne muscular dystrophy