Clinical trial
Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program (LC-FAOD DMP)
NCT04632953 is registered in ClinicalTrials.gov with Ultragenyx Pharmaceutical Inc as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program (LC-FAOD DMP)
- Lead sponsor
- Ultragenyx Pharmaceutical Inc
- Phase
- Observational
- Overall status
- Active, not recruiting
- Start date
- November 30, 2021
- Completion date
- December 31, 2035
- Enrollment
- 150 (actual)
- Sites
- 16
Conditions
As the registry lists them; a condition with its own page is linked.
long-chain fatty acid oxidation disorders (lc-faod)