Clinical trial
A Prospective, Randomized, Double-Blind, Placebo-Controlled, Single-Center Study of Oral Epalrestat Therapy in Pediatric Subjects With Phosphomannomutase 2-congenital Disorder of Glycosylation (PMM2-CDG)
NCT04925960 is registered in ClinicalTrials.gov with Maggie's Pearl, LLC as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Prospective, Randomized, Double-Blind, Placebo-Controlled, Single-Center Study of Oral Epalrestat Therapy in Pediatric Subjects With Phosphomannomutase 2-congenital Disorder of Glycosylation (PMM2-CDG)
- Lead sponsor
- Maggie's Pearl, LLC
- Phase
- Phase 3
- Overall status
- Terminated
- Start date
- November 10, 2022
- Completion date
- February 28, 2025
- Enrollment
- 42 (actual)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
phosphomannomutase 2 congenital disorder of glycosylation, phosphomannomutase 2 deficiency, phosphomannomutase ii congenital disorder of glycosylation, phosphomannomutase ii deficiency, pmm2-cdg