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Clinical trial

Effect of Enzyme Replacement Therapy in Patients With Juvenile-Onset Pompe Disease: a Long-term Observational Study

NCT04942912 is registered in ClinicalTrials.gov with Central Hospital, Nancy, France as lead sponsor.

NCT NCT04942912
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Registry record

As filed in ClinicalTrials.gov.

Title
Effect of Enzyme Replacement Therapy in Patients With Juvenile-Onset Pompe Disease: a Long-term Observational Study
Lead sponsor
Central Hospital, Nancy, France
Phase
Observational
Overall status
Unknown status
Start date
April 1, 2021
Completion date
July 30, 2021
Enrollment
10 (estimated)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

pompe's disease juvenile onset