Clinical trial
A Long-term Safety Study in Brazilian Patients With a Confirmed Diagnosis of Spinal Muscular Atrophy (SMA) Treated With Onasemnogene Abeparvovec (Zolgensma®) - ARISER Study
NCT06019637 is registered in ClinicalTrials.gov with Novartis Pharmaceuticals as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Long-term Safety Study in Brazilian Patients With a Confirmed Diagnosis of Spinal Muscular Atrophy (SMA) Treated With Onasemnogene Abeparvovec (Zolgensma®) - ARISER Study
- Lead sponsor
- Novartis Pharmaceuticals
- Phase
- Observational
- Overall status
- Recruiting
- Start date
- November 22, 2023
- Completion date
- September 30, 2038
- Enrollment
- 50 (estimated)
- Sites
- 2
Conditions
As the registry lists them; a condition with its own page is linked.
spinal muscular atrophies