Clinical trial
A Phase 1/2, Multicenter, Open-Label, Dose-Escalation, Safety, Tolerability, and Clinical Activity Study of a Single Dose of JAG201 Gene Therapy Delivered Via Intracerebroventricular Administration in Participants With SHANK3 Haploinsufficiency
NCT06662188 is registered in ClinicalTrials.gov with Jaguar Gene Therapy, LLC as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 1/2, Multicenter, Open-Label, Dose-Escalation, Safety, Tolerability, and Clinical Activity Study of a Single Dose of JAG201 Gene Therapy Delivered Via Intracerebroventricular Administration in Participants With SHANK3 Haploinsufficiency
- Lead sponsor
- Jaguar Gene Therapy, LLC
- Phase
- Phase 1/2
- Overall status
- Recruiting
- Start date
- January 7, 2024
- Completion date
- June 30, 2031
- Enrollment
- 6 (estimated)
- Sites
- 3
Conditions
As the registry lists them; a condition with its own page is linked.
phelan-mcdermid syndrome, shank3 haploinsufficiency