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Clinical trial

A Single Patient Study (SPS) of Sapropterin for Multisystem Smooth Muscle Dysfunction Syndrome (MSMDS).

NCT07574034 is registered in ClinicalTrials.gov with Gregor Andelfinger as lead sponsor.

NCT NCT07574034
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Registry record

As filed in ClinicalTrials.gov.

Title
A Single Patient Study (SPS) of Sapropterin for Multisystem Smooth Muscle Dysfunction Syndrome (MSMDS).
Lead sponsor
Gregor Andelfinger
Phase
Not applicable
Overall status
Not yet recruiting
Start date
June 1, 2026
Completion date
June 1, 2030
Enrollment
1 (estimated)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

multisystemic smooth muscle dysfunction syndrome