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Condition (MeSH)

Fucosidosis

ClinicalTrials.gov lists 10 trials for Fucosidosis or a narrower condition beneath it.

MeSH D005645 Nervous System Diseases C10 C16 C18 Listed by Orphanet as a rare disease
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Phase 1 Phase 1 1 Phase 1/2 Phase 1/2 1 Phase 2 Phase 2 3 Phase 2/3 Phase 2/3 1 Phase 3 Phase 3 1 Observational Observational 3 Phase 1 Phase 1 1 Phase 1/2 Phase 1/2 1 Phase 2 Phase 2 3 Phase 2/3 Phase 2/3 1 Phase 3 Phase 3 1 Observational Observational 3

Trials per phase

10 of the 10 trials are tagged with Fucosidosis itself; the rest are tagged with a narrower condition beneath it.

Get the Fucosidosis report as a PDF

The PDF carries up to 50 rows of each section, where the page shows the first few, with the sources listed. Enter a work email and confirm it from the message we send, and the report follows by email.

When did Fucosidosis trials start? (7)

Shown in this order: most recent first, 1990 onwards. 2026 is partial: trials registered with a 2026 start date so far, not a full year.

Trials over time, by phase

  • Phase 1
  • Phase 1/2
  • Phase 2
  • Phase 2/3
  • Phase 3
  • Observational

Top of scale: 3

1995: 1 trials (Phase 2/3 1) 1999: 1 trials (Observational 1) 2008: 3 trials (Phase 3 1, Phase 2 1, Phase 1/2 1) 2009: 2 trials (Observational 1, Phase 2 1) 2013: 1 trials (Phase 1 1) 2014: 1 trials (Phase 2 1)

Trials registered with a start date in each year, 1990 onward, stacked by phase (complete years only; the current partial year is in the table's notes). The table below lists the same counts, most recent years first.

Trials started per year
Year Trials started
2026 (partial year) 1
2014 1
2013 1
2009 2
2008 3
1999 1
1995 1

No forecast is made for this condition: it averages 0.2 trial starts a year over the five years to September, under the 5 a year the method needs.

Recruitment duration, a model prediction: none of the 10 trials evaluated at the 2026-10-09 snapshot is predicted and still running. Source: ClinicalTrials.gov / AACT (CTTI), public domain.

What phase are Fucosidosis trials in? (6)

Shown in this order: phase order.

Show the trials by phase as a table
Trials by phase
Phase Trials
Phase 1 1
Phase 1/2 1
Phase 2 3
Phase 2/3 1
Phase 3 1
Observational 3

How many Fucosidosis trials are recruiting? (5)

Shown in this order: the order a trial moves through, from not yet recruiting to unknown.

Trials by recruitment status
Status Trials
Recruiting 1
Active, not recruiting 1
Completed 5
Terminated 2
Unknown status 1

Status as registered on ClinicalTrials.gov. Each trial is counted once.

Which lead sponsors run the most Fucosidosis trials? (2)

Shown in this order: most trials first. Lead sponsors the registry classes as industry, NIH, US federal, other government or network. A hospital or university the registry files as government can appear here. Sponsors it classes as academic or other are shown on the full page, because that class cannot separate an institution from a named investigator.

Lead sponsors
Sponsor Trials
Aldagen 1
JCR Pharmaceuticals Co., Ltd. 1

Which drugs are being tested for Fucosidosis? (2)

Shown in this order: most trials first. One row per drug, matched to a single molecule under all its names, ranked by number of trials.

Drugs tested
Drug Trials
Cytoxan 2
Busulfan 2

Interventions as named in the registry (13)

Shown in this order: most trials first.

Interventions as named in the registry
Drug Trials
Alemtuzumab s.c. 2
Stem Cell Transplantation 2
cALD HR-D (High-Risk, Regimen C) 1
Allogeneic Stem Cell Transplantation 1
Human Placental Derived Stem Cell 1

These are the names sponsors entered on ClinicalTrials.gov that we have not matched to a single molecule. Some are drugs under a brand or code name; others are procedures, doses or arm labels.

Which serious adverse events do Fucosidosis trials report? (10)

Shown in this order: most subjects affected first. Subjects affected summed across trials, a cross-trial signal, not a rate.

Serious adverse events in this condition's trials
Adverse event Subjects affected Trials
Death 60 2
Auto recovery 11 2
Diarrhea 2 1
Graft failure 2 1
Pericardial Effusion 2 1

Which publications cover Fucosidosis? (1)

Shown in this order: major-topic papers first, then newest, then most linked to trials.

Publications
Publication Journal Year Major topic
Four year follow-up of a case of fucosidosis treated with unrelated donor bone marrow transplantation. Bone marrow transplantation 2001 Yes

Prevalence (12)

Shown in this order: jurisdiction, then disease name. Orphanet observation for the mapped ORPHA concept; the mapping relation column says whether that concept is exactly this condition or broader or narrower.

Prevalence
Orphanet disease Type Class Geography Jurisdiction Mapping relation
Fucosidosis Prevalence at birth 1-9 / 1 000 000 Cuba Not stated Unspecified
Fucosidosis Prevalence at birth 1-9 / 1 000 000 Cuba Not stated Exact
Fucosidosis Cases families Worldwide Not stated Exact
Fucosidosis Cases families Worldwide Not stated Unspecified
Fucosidosis Prevalence at birth 1-9 / 1 000 000 Sweden Not stated Unspecified

Rare-disease identity (2)

Shown in this order: exact, broader, narrower, other.

Rare-disease identity
Orphanet disease ORPHA code Relation Source
Fucosidosis 349 Exact Orphadata Science knowledge files, Product 1
Fucosidosis 349 Exact Orphanet Rare Disease Ontology (ORDO)

Not on this page

Not measured: delivery record.

Checked, with nothing recorded for this condition: sub-conditions in mesh.

Browse all condition evidence pages