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Condition (MeSH)

Platelet Storage Pool Deficiency

ClinicalTrials.gov lists 13 trials for Platelet Storage Pool Deficiency or a narrower condition beneath it. National Human Genome Research Institute (NHGRI) has the most among industry and government lead sponsors, with 6.

MeSH D010981 Hemic and Lymphatic Diseases C15 Listed by Orphanet as a rare disease
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Phase 1/2 Phase 1/2 1 Phase 2 Phase 2 3 Observational Observational 9 Phase 1/2 Phase 1/2 1 Phase 2 Phase 2 3 Observational Observational 9

Trials per phase

6 of the 13 trials are tagged with Platelet Storage Pool Deficiency itself; the rest are tagged with a narrower condition beneath it.

Get the Platelet Storage Pool Deficiency report as a PDF

The PDF carries up to 50 rows of each section, where the page shows the first few, with the sources listed. Enter a work email and confirm it from the message we send, and the report follows by email.

When did Platelet Storage Pool Deficiency trials start? (11)

Shown in this order: most recent first, 1990 onwards. 2026 is partial: trials registered with a 2026 start date so far, not a full year.

Trials over time, by phase

  • Phase 1/2
  • Phase 2
  • Observational

Top of scale: 2

1995: 1 trials (Observational 1) 2002: 1 trials (Observational 1) 2004: 2 trials (Observational 2) 2005: 1 trials (Phase 2 1) 2007: 2 trials (Phase 2 1, Phase 1/2 1) 2011: 1 trials (Observational 1) 2015: 1 trials (Observational 1) 2018: 1 trials (Observational 1) 2019: 1 trials (Phase 2 1) 2020: 1 trials (Observational 1) 2022: 1 trials (Observational 1)

Trials registered with a start date in each year, 1990 onward, stacked by phase (complete years only; the current partial year is in the table's notes). The table below lists the same counts, most recent years first.

Trials started per year
Year Trials started
2022 1
2020 1
2019 1
2018 1
2015 1
2011 1
2007 2
2005 1
2004 2
2002 1

No forecast is made for this condition: it averages 0.2 trial starts a year over the five years to September, under the 5 a year the method needs.

Recruitment duration, a model prediction: none of the 13 trials evaluated at the 2026-10-09 snapshot is predicted and still running. Source: ClinicalTrials.gov / AACT (CTTI), public domain.

What phase are Platelet Storage Pool Deficiency trials in? (3)

Shown in this order: phase order.

Show the trials by phase as a table
Trials by phase
Phase Trials
Phase 1/2 1
Phase 2 3
Observational 9

How many Platelet Storage Pool Deficiency trials are recruiting? (6)

Shown in this order: the order a trial moves through, from not yet recruiting to unknown.

Trials by recruitment status
Status Trials
Recruiting 2
Active, not recruiting 2
Completed 5
Terminated 1
Withdrawn 1

Status as registered on ClinicalTrials.gov. Each trial is counted once.

Which lead sponsors run the most Platelet Storage Pool Deficiency trials? (4)

Shown in this order: most trials first. Lead sponsors the registry classes as industry, NIH, US federal, other government or network. A hospital or university the registry files as government can appear here. Sponsors it classes as academic or other are shown on the full page, because that class cannot separate an institution from a named investigator.

Lead sponsors
Sponsor Trials
National Human Genome Research Institute (NHGRI) 6
23andMe, Inc. 1
National Institute of Allergy and Infectious Diseases (NIAID) 1
William Gahl, M.D. 1

Which drugs are being tested for Platelet Storage Pool Deficiency? (3)

Shown in this order: most trials first. One row per drug, matched to a single molecule under all its names, ranked by number of trials.

Drugs tested
Drug Trials
INFLIXIMAB 1
MERCAPTOPURINE 1
Zileuton 1

Interventions as named in the registry (10)

Shown in this order: most trials first.

Interventions as named in the registry
Drug Trials
Pirfenidoneone 2
Adalimumab-US 1
Pravastatin Pill 1
Low dose losartan 1
N Acetylcysteine 1

These are the names sponsors entered on ClinicalTrials.gov that we have not matched to a single molecule. Some are drugs under a brand or code name; others are procedures, doses or arm labels.

Which serious adverse events do Platelet Storage Pool Deficiency trials report? (5)

Shown in this order: most subjects affected first. Subjects affected summed across trials, a cross-trial signal, not a rate.

Serious adverse events in this condition's trials
Adverse event Subjects affected Trials
Respiratory failure 5 2
Blood creatinine phosphokinase increased 2 1
Chest pain 2 1
Deep vein thrombosis 1 1
Haematochezia 1 1

Which publications cover Platelet Storage Pool Deficiency? (1)

Shown in this order: major-topic papers first, then newest, then most linked to trials.

Publications
Publication Journal Year Major topic
Clinical and Laboratory Findings in Patients with δ-Storage Pool Disease: A Case Series. Seminars in thrombosis and hemostasis 2017 Yes

Prevalence (1)

Shown in this order: jurisdiction, then disease name. Orphanet observation for the mapped ORPHA concept; the mapping relation column says whether that concept is exactly this condition or broader or narrower.

Prevalence
Orphanet disease Type Class Geography Jurisdiction Mapping relation
Alpha delta granule deficiency Point prevalence Unknown Worldwide Not stated Unspecified

Sub-conditions in MeSH (1)

MeSH descendants one level down with at least one trial, most trials first.

Not on this page

Not measured: delivery record.

Checked, with nothing recorded for this condition: rare-disease identity.

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