Condition (MeSH)
Anemia, Hypoplastic, Congenital
ClinicalTrials.gov lists 135 trials for Anemia, Hypoplastic, Congenital or a narrower condition beneath it. National Heart, Lung, and Blood Institute (NHLBI) has the most among industry and government lead sponsors, with 9.
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Trials per phase (log scale)
1 more section with rows
4 of the 135 trials are tagged with Anemia, Hypoplastic, Congenital itself; the rest are tagged with a narrower condition beneath it.
When did Anemia, Hypoplastic, Congenital trials start? (33)
Shown in this order: most recent first, 1990 onwards. 2026 is partial: trials registered with a 2026 start date so far, not a full year. 1 trial is registered to start in 2027 or later, and not listed here.
Trials over time, by phase
- Phase 1
- Phase 1/2
- Phase 2
- Phase 2/3
- Phase 3
- Phase 4
- Not applicable
- Observational
Top of scale: 10
Trials registered with a start date in each year, 1990 onward, stacked by phase (complete years only; the current partial year is in the table's notes). The table below lists the same counts, most recent years first.
| Year | Trials started |
|---|---|
| 2026 (partial year) | 5 |
| 2025 | 2 |
| 2024 | 3 |
| 2023 | 4 |
| 2022 | 6 |
| 2021 | 2 |
| 2020 | 5 |
| 2019 | 2 |
| 2018 | 7 |
| 2017 | 6 |
Showing 10 of 33 earlier years.
No forecast is made for this condition: it averages 4.0 trial starts a year over the five years to September, under the 5 a year the method needs.
Prediction, not a registry value: median of 36 months from start to primary completion across 8 trials still running at the 2026-10-09 snapshot; registered median of 60 months across 86 trials with a primary completion typed Actual. Source: ClinicalTrials.gov / AACT (CTTI), public domain.
What phase are Anemia, Hypoplastic, Congenital trials in? (9)
Shown in this order: phase order.
Show the trials by phase as a table
| Phase | Trials |
|---|---|
| Phase 1 | 16 |
| Phase 1/2 | 26 |
| Phase 2 | 36 |
| Phase 2/3 | 4 |
| Phase 3 | 3 |
| Phase 4 | 1 |
| Not applicable | 19 |
| Observational | 28 |
| Expanded access | 2 |
How many Anemia, Hypoplastic, Congenital trials are recruiting? (9)
Shown in this order: the order a trial moves through, from not yet recruiting to unknown.
| Status | Trials |
|---|---|
| Not yet recruiting | 2 |
| Recruiting | 18 |
| Enrolling by invitation | 1 |
| Active, not recruiting | 6 |
| Available | 2 |
Showing 5 of 9 statuses.
Status as registered on ClinicalTrials.gov. Each trial is counted once.
Which lead sponsors run the most Anemia, Hypoplastic, Congenital trials? (4)
Shown in this order: most trials first. Lead sponsors the registry classes as industry, NIH, US federal, other government or network. A hospital or university the registry files as government can appear here. Sponsors it classes as academic or other are shown on the full page, because that class cannot separate an institution from a named investigator.
| Sponsor | Trials |
|---|---|
| National Heart, Lung, and Blood Institute (NHLBI) | 9 |
| Novartis Pharmaceuticals | 5 |
| National Cancer Institute (NCI) | 4 |
| Bellicum Pharmaceuticals | 3 |
Which drugs are being tested for Anemia, Hypoplastic, Congenital? (4)
Shown in this order: most trials first. One row per drug, matched to a single molecule under all its names, ranked by number of trials.
| Drug | Trials |
|---|---|
| Cytoxan | 22 |
| Busulfan | 13 |
| METHYLPREDNISOLONE | 10 |
| Melphalan | 9 |
Interventions as named in the registry (11)
Shown in this order: most trials first.
| Drug | Trials |
|---|---|
| SQ Fludarabine | 31 |
| Thymoglobulin [Anti-Thymocyte Globulin (Rabbit)] | 15 |
| Total Body Irradiation | 11 |
| Allogeneic bone marrow transplantation | 10 |
| Filgrastime (G-CSF) | 9 |
Showing 5 of 11 interventions.
These are the names sponsors entered on ClinicalTrials.gov that we have not matched to a single molecule. Some are drugs under a brand or code name; others are procedures, doses or arm labels.
Which serious adverse events do Anemia, Hypoplastic, Congenital trials report? (10)
Shown in this order: most subjects affected first. Subjects affected summed across trials, a cross-trial signal, not a rate.
| Adverse event | Subjects affected | Trials |
|---|---|---|
| Pyrexia | 37 | 7 |
| Sickle cell anaemia with crisis | 27 | 1 |
| Neutrophil count decreased | 24 | 1 |
| Infection | 23 | 7 |
| White blood cell decreased | 20 | 1 |
Showing 5 of 10 adverse events.
Sub-conditions in MeSH (2)
MeSH descendants one level down with at least one trial, most trials first.
Not on this page
Not measured: delivery record.
Checked, with nothing recorded for this condition: publications, prevalence, and rare-disease identity.