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Condition (MeSH)

Tay-Sachs Disease, AB Variant

ClinicalTrials.gov lists 2 trials for Tay-Sachs Disease, AB Variant or a narrower condition beneath it. Idorsia Pharmaceuticals Ltd. has the most among industry and government lead sponsors, with 1.

MeSH D049290 Nervous System Diseases C10 C16 C18 Listed by Orphanet as a rare disease
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Trials started per year Trials started per year 2 Trials by phase Trials by phase 1 Trials by recruitment status Trials by recruitment status 2 Lead sponsors Lead sponsors 1 Prevalence Prevalence 2 Trials started per year Trials started per year 2 Trials by phase Trials by phase 1 Trials by recruitment status Trials by recruitment status 2 Lead sponsors Lead sponsors 1 Prevalence Prevalence 2

Rows recorded per section

4 sections measured, none recorded · 1 not measured yet · 1 not computed

2 of the 2 trials are tagged with Tay-Sachs Disease, AB Variant itself; the rest are tagged with a narrower condition beneath it.

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The PDF carries up to 50 rows of each section, where the page shows the first few, with the sources listed. Enter a work email and confirm it from the message we send, and the report follows by email.

When did Tay-Sachs Disease, AB Variant trials start? (2)

Shown in this order: most recent first, 1990 onwards. 2026 is partial: trials registered with a 2026 start date so far, not a full year.

Trials started per year
Year Trials started
2020 1
2019 1

No forecast is made for this condition: it averages 0.0 trial starts a year over the five years to September, under the 5 a year the method needs.

Recruitment duration, a model prediction: none of the 2 trials evaluated at the 2026-10-09 snapshot is predicted and still running. Source: ClinicalTrials.gov / AACT (CTTI), public domain.

What phase are Tay-Sachs Disease, AB Variant trials in? (1)

Shown in this order: phase order.

Trials by phase
Phase Trials
Observational 2

How many Tay-Sachs Disease, AB Variant trials are recruiting? (2)

Shown in this order: the order a trial moves through, from not yet recruiting to unknown.

Trials by recruitment status
Status Trials
Completed 1
Unknown status 1

Status as registered on ClinicalTrials.gov. Each trial is counted once.

Which lead sponsors run the most Tay-Sachs Disease, AB Variant trials? (1)

Shown in this order: most trials first. Lead sponsors the registry classes as industry, NIH, US federal, other government or network. A hospital or university the registry files as government can appear here. Sponsors it classes as academic or other are shown on the full page, because that class cannot separate an institution from a named investigator.

Lead sponsors
Sponsor Trials
Idorsia Pharmaceuticals Ltd. 1

Prevalence (2)

Shown in this order: jurisdiction, then disease name. Orphanet observation for the mapped ORPHA concept; the mapping relation column says whether that concept is exactly this condition or broader or narrower.

Prevalence
Orphanet disease Type Class Geography Jurisdiction Mapping relation
GM2 gangliosidosis, AB variant Cases families Worldwide Not stated Unspecified
GM2 gangliosidosis, AB variant Point prevalence <1 / 1 000 000 Worldwide Not stated Unspecified

Not on this page

Not measured: delivery record.

Checked, with nothing recorded for this condition: serious adverse events in this condition's trials, publications, rare-disease identity, and sub-conditions in mesh.

Not computed for conditions with fewer than 10 trials: drugs tested.

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