Clinical trial
Prospective, Open-label, Single-arm, Exploratory Study of the Effect and Safety of rhGAA in Patients With Advanced Late-onset Pompe Disease Who Are Receiving Respiratory Support
NCT00268944 is registered in ClinicalTrials.gov with Genzyme, a Sanofi Company as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Prospective, Open-label, Single-arm, Exploratory Study of the Effect and Safety of rhGAA in Patients With Advanced Late-onset Pompe Disease Who Are Receiving Respiratory Support
- Lead sponsor
- Genzyme, a Sanofi Company
- Phase
- Phase 3
- Overall status
- Completed
- Start date
- December 31, 2005
- Completion date
- June 30, 2007
- Enrollment
- 5 (actual)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
acid maltase deficiency disease, glycogen storage disease type ii (gsd-ii), glycogenosis 2, pompe disease (late-onset)