Clinical trial
Preclinical & Phase I/II Trials of AAV-AAT Vectors: Phase I Trial of Intramuscular Injection of a Recombinant Adeno-Associated Virus Alpha 1-Antitrypsin (rAAV2-CB-hAAT) Gene Vector to AAT-Deficient Adults
NCT00377416 is registered in ClinicalTrials.gov with University of Massachusetts, Worcester as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Preclinical & Phase I/II Trials of AAV-AAT Vectors: Phase I Trial of Intramuscular Injection of a Recombinant Adeno-Associated Virus Alpha 1-Antitrypsin (rAAV2-CB-hAAT) Gene Vector to AAT-Deficient Adults
- Lead sponsor
- University of Massachusetts, Worcester
- Phase
- Phase 1
- Overall status
- Completed
- Start date
- March 31, 2004
- Completion date
- January 31, 2020
- Enrollment
- 12 (actual)
- Sites
- 2
Conditions
As the registry lists them; a condition with its own page is linked.