Clinical trial
A Multicenter, Multinational, Longitudinal Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
NCT00787995 is registered in ClinicalTrials.gov with BioMarin Pharmaceutical as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Multicenter, Multinational, Longitudinal Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
- Lead sponsor
- BioMarin Pharmaceutical
- Phase
- Observational
- Overall status
- Terminated
- Start date
- October 31, 2008
- Completion date
- July 31, 2014
- Enrollment
- 353 (actual)
- Sites
- 15
Conditions
As the registry lists them; a condition with its own page is linked.
morquio a syndrome, mps iv a, mucopolysaccharidosis iva