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Clinical trial

Phase I/II, Historical Controlled, Open-label, Non-randomised, Single-centre Trial to Assess the Safety and Efficacy of EF1αS-ADA Lentiviral Vector Mediated Gene Modification of Autologous CD34+ Cells From ADA-deficient Individuals

NCT01380990 is registered in ClinicalTrials.gov with Great Ormond Street Hospital for Children NHS Foundation Trust as lead sponsor.

NCT NCT01380990
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Registry record

As filed in ClinicalTrials.gov.

Title
Phase I/II, Historical Controlled, Open-label, Non-randomised, Single-centre Trial to Assess the Safety and Efficacy of EF1αS-ADA Lentiviral Vector Mediated Gene Modification of Autologous CD34+ Cells From ADA-deficient Individuals
Lead sponsor
Great Ormond Street Hospital for Children NHS Foundation Trust
Phase
Phase 1/2
Overall status
Completed
Start date
November 15, 2012
Completion date
December 23, 2019
Enrollment
36 (actual)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

adenosine deaminase deficiency, severe combined immunodeficiencies (scid)