Clinical trial
A Study of EZN-2279 (Polyethylene Glycol Recombinant Adenosine Deaminase [PEG-rADA]) Administered as a Weekly Intramuscular Injection in Patients With Adenosine Deaminase (ADA)-Deficient Combined Immunodeficiency
NCT01420627 is registered in ClinicalTrials.gov with Leadiant Biosciences, Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Study of EZN-2279 (Polyethylene Glycol Recombinant Adenosine Deaminase [PEG-rADA]) Administered as a Weekly Intramuscular Injection in Patients With Adenosine Deaminase (ADA)-Deficient Combined Immunodeficiency
- Lead sponsor
- Leadiant Biosciences, Inc.
- Phase
- Phase 3
- Overall status
- Completed
- Start date
- January 24, 2014
- Completion date
- May 29, 2019
- Enrollment
- 7 (actual)
- Sites
- 6
Conditions
As the registry lists them; a condition with its own page is linked.
ada-scid, adenosine deaminase deficiency, severe combined immunodeficiency