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Clinical trial

A Phase I/II Clinical Trial of Hematopoietic Stem Cell Gene Therapy for the Treatment of Metachromatic Leukodystrophy

NCT01560182 is registered in ClinicalTrials.gov with Orchard Therapeutics as lead sponsor.

NCT NCT01560182
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Registry record

As filed in ClinicalTrials.gov.

Title
A Phase I/II Clinical Trial of Hematopoietic Stem Cell Gene Therapy for the Treatment of Metachromatic Leukodystrophy
Lead sponsor
Orchard Therapeutics
Phase
Phase 1/2
Overall status
Completed
Start date
April 9, 2010
Completion date
September 19, 2025
Enrollment
20 (actual)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

lysosomal storage disease, metachromatic leukodystrophy