Clinical trial
A Phase 2, Open Label, Multicenter Study to Evaluate the Safety, Tolerability, Efficacy, and Pharmacokinetics of Sebelipase Alfa in Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency
NCT02193867 is registered in ClinicalTrials.gov with Alexion Pharmaceuticals, Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 2, Open Label, Multicenter Study to Evaluate the Safety, Tolerability, Efficacy, and Pharmacokinetics of Sebelipase Alfa in Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency
- Lead sponsor
- Alexion Pharmaceuticals, Inc.
- Phase
- Phase 2
- Overall status
- Terminated
- Start date
- June 6, 2014
- Completion date
- October 30, 2018
- Enrollment
- 10 (actual)
- Sites
- 5
Conditions
As the registry lists them; a condition with its own page is linked.
lysosomal acid lipase deficiency