Clinical trial
A Randomized, Placebo-Controlled, Blind-Start, Single-Crossover Phase 3 Study to Assess the Efficacy and Safety of UX003 rhGUS Enzyme Replacement Therapy in Patients With MPS 7
NCT02230566 is registered in ClinicalTrials.gov with Ultragenyx Pharmaceutical Inc as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Randomized, Placebo-Controlled, Blind-Start, Single-Crossover Phase 3 Study to Assess the Efficacy and Safety of UX003 rhGUS Enzyme Replacement Therapy in Patients With MPS 7
- Lead sponsor
- Ultragenyx Pharmaceutical Inc
- Phase
- Phase 3
- Overall status
- Completed
- Start date
- December 31, 2014
- Completion date
- May 31, 2016
- Enrollment
- 12 (actual)
- Sites
- 4
Conditions
As the registry lists them; a condition with its own page is linked.
mps 7, mps vii, mucopolysaccharidosis, sly syndrome