Clinical trial
Augmentation of Umbilical Cord Blood Transplantation for Inherited Metabolic Diseases With Intrathecal Administration of Human Umbilical Cord Blood-Derived Oligodendrocyte-Like Cells
NCT02254863 is registered in ClinicalTrials.gov with Joanne Kurtzberg, MD as lead sponsor.
Search trials, sites, companies and investigators, and follow each one to the others. Individual plan, $249/seat/mo. Card required.
Registry record
As filed in ClinicalTrials.gov.
- Title
- Augmentation of Umbilical Cord Blood Transplantation for Inherited Metabolic Diseases With Intrathecal Administration of Human Umbilical Cord Blood-Derived Oligodendrocyte-Like Cells
- Lead sponsor
- Joanne Kurtzberg, MD
- Phase
- Phase 1
- Overall status
- Recruiting
- Start date
- September 30, 2014
- Completion date
- October 31, 2027
- Enrollment
- 40 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
adrenoleukodystrophy, alpha-mannosidosis, batten disease, brain diseases, metabolic, inborn, leukodystrophy, globoid cell, leukodystrophy, metachromatic, mucopolysaccharidosis ii, neimann pick disease, pelizaeus-merzbacher disease, sandhoff disease, sanfilippo mucopolysaccharidoses, tay-sachs disease