Clinical trial
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
NCT02294877 is registered in ClinicalTrials.gov with BioMarin Pharmaceutical as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
- Lead sponsor
- BioMarin Pharmaceutical
- Phase
- Observational
- Overall status
- Completed
- Start date
- September 30, 2014
- Completion date
- February 21, 2024
- Enrollment
- 418 (actual)
- Sites
- 79
Conditions
As the registry lists them; a condition with its own page is linked.
morquio a syndrome, mps iva, mucopolysaccharidosis iv type a