Clinical trial
Expanded Access Protocol of Patisiran for Patients With Hereditary Transthyretin-Mediated Amyloidosis (hATTR Amyloidosis) With Polyneuropathy
NCT02939820 is registered in ClinicalTrials.gov with Alnylam Pharmaceuticals as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Expanded Access Protocol of Patisiran for Patients With Hereditary Transthyretin-Mediated Amyloidosis (hATTR Amyloidosis) With Polyneuropathy
- Lead sponsor
- Alnylam Pharmaceuticals
- Phase
- Expanded access
- Overall status
- Approved for marketing
- Start date
- Not reported
- Completion date
- Not reported
- Enrollment
- Not reported
- Sites
- Not reported
Conditions
As the registry lists them; a condition with its own page is linked.
amyloid neuropathies, amyloid neuropathies, familial, amyloidosis, hereditary, amyloidosis, hereditary, transthyretin-related, familial amyloid polyneuropathies, ttr-mediated amyloidosis