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Clinical trial

A Multicenter, Observational, Prospective, Natural History Study of Homocystinuria Due to Cystathionine Beta-synthase Deficiency in Pediatric and Adult Patients (ACAPPELLA)

NCT02998710 is registered in ClinicalTrials.gov with Travere Therapeutics, Inc. as lead sponsor.

NCT NCT02998710
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Registry record

As filed in ClinicalTrials.gov.

Title
A Multicenter, Observational, Prospective, Natural History Study of Homocystinuria Due to Cystathionine Beta-synthase Deficiency in Pediatric and Adult Patients (ACAPPELLA)
Lead sponsor
Travere Therapeutics, Inc.
Phase
Observational
Overall status
Completed
Start date
January 31, 2017
Completion date
July 31, 2026
Enrollment
110 (actual)
Sites
11

Conditions

As the registry lists them; a condition with its own page is linked.

homocystinuria due to cbs deficiency