Clinical trial
A Phase 1/2, Open-Label Safety and Dose-Finding Study of Adeno-Associated Virus (AAV) Serotype 8 (AAV8)-Mediated Gene Transfer of Glucose-6- Phosphatase (G6Pase) in Adults With Glycogen Storage Disease Type Ia (GSDIa)
NCT03517085 is registered in ClinicalTrials.gov with Ultragenyx Pharmaceutical Inc as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 1/2, Open-Label Safety and Dose-Finding Study of Adeno-Associated Virus (AAV) Serotype 8 (AAV8)-Mediated Gene Transfer of Glucose-6- Phosphatase (G6Pase) in Adults With Glycogen Storage Disease Type Ia (GSDIa)
- Lead sponsor
- Ultragenyx Pharmaceutical Inc
- Phase
- Phase 1/2
- Overall status
- Completed
- Start date
- May 18, 2018
- Completion date
- November 2, 2021
- Enrollment
- 12 (actual)
- Sites
- 6
Conditions
As the registry lists them; a condition with its own page is linked.
gsd1