Clinical trial
A Phase 3, Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy and Safety of AG-348 in Not Regularly Transfused Adult Subjects With Pyruvate Kinase Deficiency
NCT03548220 is registered in ClinicalTrials.gov with Agios Pharmaceuticals, Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 3, Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy and Safety of AG-348 in Not Regularly Transfused Adult Subjects With Pyruvate Kinase Deficiency
- Lead sponsor
- Agios Pharmaceuticals, Inc.
- Phase
- Phase 3
- Overall status
- Completed
- Start date
- August 9, 2018
- Completion date
- October 9, 2020
- Enrollment
- 80 (actual)
- Sites
- 46
Conditions
As the registry lists them; a condition with its own page is linked.
anemia, hemolytic, pyruvate kinase deficiency