Clinical trial
A Phase 1/2/3 Multicenter, Open-Label Study to Evaluate the Efficacy, Safety, Tolerability, and Pharmacodynamics of RGX-121 in Pediatric Subjects With MPS II (Hunter Syndrome)
NCT03566043 is registered in ClinicalTrials.gov with REGENXBIO Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 1/2/3 Multicenter, Open-Label Study to Evaluate the Efficacy, Safety, Tolerability, and Pharmacodynamics of RGX-121 in Pediatric Subjects With MPS II (Hunter Syndrome)
- Lead sponsor
- REGENXBIO Inc.
- Phase
- Phase 2/3
- Overall status
- Active, not recruiting
- Start date
- September 27, 2018
- Completion date
- August 31, 2025
- Enrollment
- 48 (estimated)
- Sites
- 5
Conditions
As the registry lists them; a condition with its own page is linked.
mucopolysaccharidosis type ii (mps ii)