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Clinical trial

Effects of N-Acetyl-L-Leucine on GM2 Gangliosidosis (Tay-Sachs and Sandhoff Disease): A Multinational, Multicenter, Open-label, Rater-blinded Phase II Study

NCT03759665 is registered in ClinicalTrials.gov with IntraBio Inc as lead sponsor.

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Registry record

As filed in ClinicalTrials.gov.

Title
Effects of N-Acetyl-L-Leucine on GM2 Gangliosidosis (Tay-Sachs and Sandhoff Disease): A Multinational, Multicenter, Open-label, Rater-blinded Phase II Study
Lead sponsor
IntraBio Inc
Phase
Phase 2
Overall status
Completed
Start date
June 7, 2019
Completion date
January 9, 2023
Enrollment
30 (actual)
Sites
8

Conditions

As the registry lists them; a condition with its own page is linked.

gm2 gangliosidosis, sandhoff disease, tay-sachs disease