Clinical trial
Cellular Pharmacodynamics of Small Molecules in Sanfilippo Disease(s) (MPS3) and Other Lysosomal Storage Disorders
NCT03812055 is registered in ClinicalTrials.gov with Lysosomal and Rare Disorders Research and Treatment Center, Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Cellular Pharmacodynamics of Small Molecules in Sanfilippo Disease(s) (MPS3) and Other Lysosomal Storage Disorders
- Lead sponsor
- Lysosomal and Rare Disorders Research and Treatment Center, Inc.
- Phase
- Observational
- Overall status
- Unknown status
- Start date
- July 6, 2018
- Completion date
- July 31, 2020
- Enrollment
- 50 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.