Clinical trial
A Multi-Center, Low-Interventional Study With a Retrospective Component in Participants With Late-Onset Pompe Disease
NCT03893240 is registered in ClinicalTrials.gov with Spark Therapeutics, Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Multi-Center, Low-Interventional Study With a Retrospective Component in Participants With Late-Onset Pompe Disease
- Lead sponsor
- Spark Therapeutics, Inc.
- Phase
- Not applicable
- Overall status
- Completed
- Start date
- June 12, 2019
- Completion date
- October 27, 2020
- Enrollment
- 61 (actual)
- Sites
- 18
Conditions
As the registry lists them; a condition with its own page is linked.
acid maltase deficiency, glycogen storage disease type 2, lopd, lysosomal storage diseases, pompe disease, pompe disease (late-onset)