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Clinical trial

A Multi-Center, Low-Interventional Study With a Retrospective Component in Participants With Late-Onset Pompe Disease

NCT03893240 is registered in ClinicalTrials.gov with Spark Therapeutics, Inc. as lead sponsor.

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Registry record

As filed in ClinicalTrials.gov.

Title
A Multi-Center, Low-Interventional Study With a Retrospective Component in Participants With Late-Onset Pompe Disease
Lead sponsor
Spark Therapeutics, Inc.
Phase
Not applicable
Overall status
Completed
Start date
June 12, 2019
Completion date
October 27, 2020
Enrollment
61 (actual)
Sites
18

Conditions

As the registry lists them; a condition with its own page is linked.

acid maltase deficiency, glycogen storage disease type 2, lopd, lysosomal storage diseases, pompe disease, pompe disease (late-onset)