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Clinical trial

Phase 2 Active Treatment Study to Evaluate the Efficacy and Safety of SRK-015 in Patients With Later-Onset Spinal Muscular Atrophy (TOPAZ)

NCT03921528 is registered in ClinicalTrials.gov with Scholar Rock, Inc. as lead sponsor.

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Registry record

As filed in ClinicalTrials.gov.

Title
Phase 2 Active Treatment Study to Evaluate the Efficacy and Safety of SRK-015 in Patients With Later-Onset Spinal Muscular Atrophy (TOPAZ)
Lead sponsor
Scholar Rock, Inc.
Phase
Phase 2
Overall status
Completed
Start date
April 22, 2019
Completion date
February 28, 2024
Enrollment
58 (actual)
Sites
16

Conditions

As the registry lists them; a condition with its own page is linked.

atrophy, muscular atrophy, muscular atrophy, spinal, neuromuscular diseases, neuromuscular manifestations, sma, spinal muscular atrophy, spinal muscular atrophy type 2, spinal muscular atrophy type 3