Clinical trial
An Observational Long-term Follow-up Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency (ADA-SCID)
NCT04049084 is registered in ClinicalTrials.gov with University of California, Los Angeles as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- An Observational Long-term Follow-up Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency (ADA-SCID)
- Lead sponsor
- University of California, Los Angeles
- Phase
- Observational
- Overall status
- Enrolling by invitation
- Start date
- September 26, 2019
- Completion date
- August 31, 2040
- Enrollment
- 70 (estimated)
- Sites
- 2
Conditions
As the registry lists them; a condition with its own page is linked.
adenosine deaminase deficiency, severe combined immunodeficiency (scid)