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Clinical trial

Evaluate the Long Term Effectiveness & Safety of the Use of Carglumic Acid (Carbaglu®) in Patients With Propionic Acidemia (PA) or Methylmalonic Acidemia (MMA).

NCT04284917 is registered in ClinicalTrials.gov with National Taiwan University Hospital as lead sponsor.

NCT NCT04284917
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Registry record

As filed in ClinicalTrials.gov.

Title
Evaluate the Long Term Effectiveness & Safety of the Use of Carglumic Acid (Carbaglu®) in Patients With Propionic Acidemia (PA) or Methylmalonic Acidemia (MMA).
Lead sponsor
National Taiwan University Hospital
Phase
Not applicable
Overall status
Completed
Start date
November 28, 2019
Completion date
March 11, 2025
Enrollment
3 (actual)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

propionic acidemia (pa) , methylmalonic acidemia (mma)