Clinical trial
GSD VI and GSD IX Natural History
NCT04454216 is registered in ClinicalTrials.gov with Duke University as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- GSD VI and GSD IX Natural History
- Lead sponsor
- Duke University
- Phase
- Observational
- Overall status
- Recruiting
- Start date
- September 18, 2020
- Completion date
- January 1, 2030
- Enrollment
- 400 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
glycogen storage disease ixa1, glycogen storage disease ixa2, glycogen storage disease ixb, glycogen storage disease ixc, glycogen storage disease vi, gsd 6, gsd 9 (all subtypes)