Clinical trial
Cerliponase Alfa Observational Study
NCT04476862 is registered in ClinicalTrials.gov with BioMarin Pharmaceutical as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Cerliponase Alfa Observational Study
- Lead sponsor
- BioMarin Pharmaceutical
- Phase
- Observational
- Overall status
- Active, not recruiting
- Start date
- August 19, 2020
- Completion date
- August 31, 2030
- Enrollment
- 35 (estimated)
- Sites
- 16
Conditions
As the registry lists them; a condition with its own page is linked.
late-infantile neuronal ceroid lipofuscinosis type 2