Clinical trial
Pyruvate Kinase Deficiency Global Longitudinal Registry: Patient-Reported Outcomes
NCT04964323 is registered in ClinicalTrials.gov with Agios Pharmaceuticals, Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Pyruvate Kinase Deficiency Global Longitudinal Registry: Patient-Reported Outcomes
- Lead sponsor
- Agios Pharmaceuticals, Inc.
- Phase
- Observational
- Overall status
- Terminated
- Start date
- July 2, 2021
- Completion date
- June 30, 2023
- Enrollment
- 15 (actual)
- Sites
- 5
Conditions
As the registry lists them; a condition with its own page is linked.
anemia, anemia, hemolytic, pyruvate kinase deficiency, pyruvate kinase deficiency anemia