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Clinical trial

A Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of Adeno-Associated Virus Serotype 8-Mediated Gene Transfer of Glucose-6-Phosphatase in Patients With Glycogen Storage Disease Type Ia

NCT05139316 is registered in ClinicalTrials.gov with Ultragenyx Pharmaceutical Inc as lead sponsor.

NCT NCT05139316
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Registry record

As filed in ClinicalTrials.gov.

Title
A Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of Adeno-Associated Virus Serotype 8-Mediated Gene Transfer of Glucose-6-Phosphatase in Patients With Glycogen Storage Disease Type Ia
Lead sponsor
Ultragenyx Pharmaceutical Inc
Phase
Phase 3
Overall status
Completed
Start date
November 8, 2021
Completion date
February 20, 2026
Enrollment
52 (actual)
Sites
20

Conditions

As the registry lists them; a condition with its own page is linked.

glycogen storage disease type ia