Clinical trial
Antisense Oligonucleotide Therapy in Spinal Muscular Atrophy: An Observational Study in China
NCT05187260 is registered in ClinicalTrials.gov with First Affiliated Hospital of Fujian Medical University as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Antisense Oligonucleotide Therapy in Spinal Muscular Atrophy: An Observational Study in China
- Lead sponsor
- First Affiliated Hospital of Fujian Medical University
- Phase
- Observational
- Overall status
- Unknown status
- Start date
- January 1, 2022
- Completion date
- January 31, 2024
- Enrollment
- 1,000 (estimated)
- Sites
- 3
Conditions
As the registry lists them; a condition with its own page is linked.
spinal muscular atrophy