Clinical trial
Acid Sphingomyelinase Deficiency (ASMD): Data Analysis of Adult and Pediatric Patients on Early Access to Olipudase Alfa in France
NCT05359276 is registered in ClinicalTrials.gov with Sanofi as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Acid Sphingomyelinase Deficiency (ASMD): Data Analysis of Adult and Pediatric Patients on Early Access to Olipudase Alfa in France
- Lead sponsor
- Sanofi
- Phase
- Observational
- Overall status
- Completed
- Start date
- June 10, 2022
- Completion date
- December 31, 2024
- Enrollment
- 40 (actual)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
acid sphingomyelinase deficiency (asmd)