Clinical trial
Protocol-LATAM RegistrAME: Longitudinal Data Collection in Pediatric and Adult Patients With Spinal Muscular Atrophy in Latin America - a Regional Registry
NCT05475691 is registered in ClinicalTrials.gov with Hospital Israelita Albert Einstein as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Protocol-LATAM RegistrAME: Longitudinal Data Collection in Pediatric and Adult Patients With Spinal Muscular Atrophy in Latin America - a Regional Registry
- Lead sponsor
- Hospital Israelita Albert Einstein
- Phase
- Observational
- Overall status
- Unknown status
- Start date
- August 17, 2022
- Completion date
- January 30, 2025
- Enrollment
- 361 (actual)
- Sites
- 18
Conditions
As the registry lists them; a condition with its own page is linked.
spinal muscular atrophy