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Clinical trial

An Open-Label, Non-Comparative Clinical Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene (ANB-004 (JSC BIOCAD, Russia)) After a Single Intravenous Administration of Escalating Doses in Children With Spinal Muscular Atrophy

NCT05747261 is registered in ClinicalTrials.gov with Biocad as lead sponsor.

NCT NCT05747261
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Registry record

As filed in ClinicalTrials.gov.

Title
An Open-Label, Non-Comparative Clinical Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene (ANB-004 (JSC BIOCAD, Russia)) After a Single Intravenous Administration of Escalating Doses in Children With Spinal Muscular Atrophy
Lead sponsor
Biocad
Phase
Phase 1/2
Overall status
Recruiting
Start date
February 2, 2023
Completion date
August 31, 2030
Enrollment
40 (estimated)
Sites
7

Conditions

As the registry lists them; a condition with its own page is linked.

spinal muscular atrophy (sma)