Clinical trial
MAP THE SMA: a Machine-learning Based Algorithm to Predict THErapeutic Response in Spinal Muscular Atrophy
NCT05769465 is registered in ClinicalTrials.gov with Fondazione Policlinico Universitario Agostino Gemelli IRCCS as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- MAP THE SMA: a Machine-learning Based Algorithm to Predict THErapeutic Response in Spinal Muscular Atrophy
- Lead sponsor
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- Phase
- Observational
- Overall status
- Unknown status
- Start date
- April 1, 2023
- Completion date
- April 1, 2026
- Enrollment
- 247 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
spinal muscular atrophy