Clinical trial
Personalized Medicine for Spinal Muscular Atrophy: a Translational Project to Achieve Patient Specific Therapeutic Guidance.
NCT05779956 is registered in ClinicalTrials.gov with Fondazione Policlinico Universitario Agostino Gemelli IRCCS as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Personalized Medicine for Spinal Muscular Atrophy: a Translational Project to Achieve Patient Specific Therapeutic Guidance.
- Lead sponsor
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- Phase
- Observational
- Overall status
- Unknown status
- Start date
- September 1, 2021
- Completion date
- August 31, 2024
- Enrollment
- 90 (estimated)
- Sites
- 2
Conditions
As the registry lists them; a condition with its own page is linked.
spinal muscular atrophy