Clinical trial
A Multicenter, Open Label, Randomized, Dose-Escalation and Dose-Expansion Study of the Safety, Tolerability, and Efficacy of a Single Intrathecal Administration of TSHA-102, an AAV9-Delivered Gene Therapy, for the Treatment of Pediatric Females With Rett Syndrome
NCT06152237 is registered in ClinicalTrials.gov with Taysha Gene Therapies, Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Multicenter, Open Label, Randomized, Dose-Escalation and Dose-Expansion Study of the Safety, Tolerability, and Efficacy of a Single Intrathecal Administration of TSHA-102, an AAV9-Delivered Gene Therapy, for the Treatment of Pediatric Females With Rett Syndrome
- Lead sponsor
- Taysha Gene Therapies, Inc.
- Phase
- Phase 1/2
- Overall status
- Active, not recruiting
- Start date
- December 12, 2023
- Completion date
- November 2, 2031
- Enrollment
- 6 (actual)
- Sites
- 5
Conditions
As the registry lists them; a condition with its own page is linked.