Clinical trial
A Phase 1/2, Multicenter, Open-Label Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A)
NCT06181136 is registered in ClinicalTrials.gov with Denali Therapeutics Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 1/2, Multicenter, Open-Label Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A)
- Lead sponsor
- Denali Therapeutics Inc.
- Phase
- Phase 1/2
- Overall status
- Active, not recruiting
- Start date
- December 7, 2023
- Completion date
- August 31, 2028
- Enrollment
- 20 (actual)
- Sites
- 4
Conditions
As the registry lists them; a condition with its own page is linked.
mucopolysaccharidosis type iiia