Clinical trial
A Prospective, Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in Hereditary Tyrosinemia Type 1 (HT-1) Patients in Routine Clinical Care in China
NCT06227429 is registered in ClinicalTrials.gov with Swedish Orphan Biovitrum as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Prospective, Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in Hereditary Tyrosinemia Type 1 (HT-1) Patients in Routine Clinical Care in China
- Lead sponsor
- Swedish Orphan Biovitrum
- Phase
- Observational
- Overall status
- Withdrawn
- Start date
- September 30, 2025
- Completion date
- June 30, 2027
- Enrollment
- 0 (actual)
- Sites
- 4
Conditions
As the registry lists them; a condition with its own page is linked.
hereditary tyrosinemia, type i