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Clinical trial

A Long-term Extension Trial Investigating the Safety and Efficacy of GTX-102 in Patients With Angelman Syndrome

NCT06415344 is registered in ClinicalTrials.gov with Ultragenyx Pharmaceutical Inc as lead sponsor.

NCT NCT06415344
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Registry record

As filed in ClinicalTrials.gov.

Title
A Long-term Extension Trial Investigating the Safety and Efficacy of GTX-102 in Patients With Angelman Syndrome
Lead sponsor
Ultragenyx Pharmaceutical Inc
Phase
Phase 3
Overall status
Active, not recruiting
Start date
July 31, 2024
Completion date
February 28, 2029
Enrollment
255 (estimated)
Sites
23

Conditions

As the registry lists them; a condition with its own page is linked.

angelman syndrome