Clinical trial
A Phase 3, Randomized, Multicenter, Double-Blind, Placebo-Controlled Study of Acoramidis for Transthyretin Amyloidosis Prevention in the Young (ACT-EARLY Trial)
NCT06563895 is registered in ClinicalTrials.gov with Eidos Therapeutics, a BridgeBio company as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 3, Randomized, Multicenter, Double-Blind, Placebo-Controlled Study of Acoramidis for Transthyretin Amyloidosis Prevention in the Young (ACT-EARLY Trial)
- Lead sponsor
- Eidos Therapeutics, a BridgeBio company
- Phase
- Phase 3
- Overall status
- Recruiting
- Start date
- May 12, 2025
- Completion date
- December 31, 2032
- Enrollment
- 587 (estimated)
- Sites
- 104
Conditions
As the registry lists them; a condition with its own page is linked.
amyloid cardiomyopathy, amyloidosis, cardiomyopathies, heart diseases, polyneuropathies, transthyretin amyloidosis