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Clinical trial

An Adaptive Design Basket Trial of Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

NCT06647979 is registered in ClinicalTrials.gov with Daniel Bauer as lead sponsor.

NCT NCT06647979
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Registry record

As filed in ClinicalTrials.gov.

Title
An Adaptive Design Basket Trial of Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies
Lead sponsor
Daniel Bauer
Phase
Phase 1
Overall status
Recruiting
Start date
December 1, 2025
Completion date
December 31, 2030
Enrollment
10 (estimated)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

beta-thalassemia, sickle cell anemia (hbss, or hbsβ-thalassemia0), sickle cell disease, transfusion dependent beta-thalassaemia